FDA accepts sNDA for higher regimen nusinersen for spinal muscular atrophy

Published Date: 30 Jan 2025

The higher dose regimen of nusinersen comprises a more rapid loading regimen, two 50 mg doses 14 days apart, and higher maintenance regimen, 28 mg, every 4 months.

Read Full News

Latest News

US Senator Durbin Urges RFK Jr. to Resist Easing Vape Rules

U.S. Senator Dick Durbin urged Health Secretary Robert F. Kennedy Jr. on Wednesday to resist an easing of rules on ⁠flavoured vapes, saying the moves were short-sighted and...

US Health Secretary Kennedy Fires Heads Of Key Preventive Health Panel

U.S. Health Secretary Robert F. Kennedy Jr. fired the chair and vice chair of the influential task force that decides what preventive medical care should be ⁠provided at no...

Spinal Anesthesia for Circumcision Tops General Anesthesia

Spinal anesthesia offers faster recovery, similar OR time, and significantly less opioid use, with no increase in cost or OR delays.

Vegetarian Diet in Kids Not Linked to More Nutrition Risk

Though no association was seen between eating a vegetarian diet and nutrition risk, there were too few vegan children in the study to assess their nutrition risk.

Cash Transfers Cut Infant Maltreatment Reports

A universal prenatal and infant cash prescription program was associated with a decrease in investigated maltreatment allegations within the first 6 months of life.

The ITP Expert Exchange: Translating Evidence Into Evolving Practice

The ITP Expert Exchange: Translating Evidence Into Evolving Practice

Todays Updates

EMA Backs Breast Cancer SERD After FDA No Vote

The recommendation follows phase 3 data showing longer progression-free survival when patients switched to camizestrant plus a CDK4/6 inhibitor.

Datopotamab Deruxtecan Earns New Breast Cancer Indication

The antibody drug conjugate was approved by the FDA for certain patients with triple-negative breast cancer.

Todays Updates

EMA Backs Breast Cancer SERD After FDA No Vote

The recommendation follows phase 3 data showing longer progression-free survival when patients switched to camizestrant plus a CDK4/6 inhibitor.

Datopotamab Deruxtecan Earns New Breast Cancer Indication

The antibody drug conjugate was approved by the FDA for certain patients with triple-negative breast cancer.

Latest News

U.S. Senator Dick Durbin urged Health Secretary Robert F. Kennedy Jr. on Wednesday to resist an easing of rules on ⁠flavoured vapes, saying the moves were short-sighted and...

U.S. Health Secretary Robert F. Kennedy Jr. fired the chair and vice chair of the influential task force that decides what preventive medical care should be ⁠provided at no...

Spinal anesthesia offers faster recovery, similar OR time, and significantly less opioid use, with no increase in cost or OR delays.

Though no association was seen between eating a vegetarian diet and nutrition risk, there were too few vegan children in the study to assess their nutrition risk.

A universal prenatal and infant cash prescription program was associated with a decrease in investigated maltreatment allegations within the first 6 months of life.

The ITP Expert Exchange: Translating Evidence Into Evolving Practice

News All Time

RFK Jr. Faced Congress. A Physician-Senator's Competing Loyalties Were on Display.

Bill Cassidy, who is seeking reelection, walked a fine line

Vaccines, Budget Cuts, Affordability: Takeaways From RFK Jr.'s Gauntlet of Hearings

Kennedy acknowledged some HHS cuts are "painful"

Kids With Chronic Health, Social Needs More Likely to Frequently Miss School

Weighted study sample represented more than 49 million U.S. kids

South Carolina's Measles Outbreak Is Over After Sickening Nearly 1,000 People

But health officials are still on guard

FDA Analysis Says Infant Formula Supply Is Safe After Testing for Contaminants

"There's no reason not to use any available formula," said one expert

Chocolate Product Recall; Trump Admin Fights Vaccine Ruling; Measles in Travelers

Health news and commentary gathered by MedPage Today staff

New Maintenance Option Approved for Asthma

Breztri becomes the first single-inhaler triple therapy for patients as young as 12 years

Trump's New Surgeon General Pick Has Both Praised and Cringed at His Administration

Nicole Saphier is a radiologist and former Fox News Channel contributor

Telemedicine Visits Tied to Fewer Antibiotics for Respiratory Infections

Findings for virtual visits with primary care suggested high quality

Did Newborn Die From Mom's Marijuana Use?

Diagnosis of exclusion leads to answer of... probably

Teen Seeks Care for Delayed Growth Compared With His Twin

Case shows confluence of hormone therapy cost and limited resources in developing areas

This Common Household Product Tied to Kid's Seizures

Investigation revealed the likely cause of salicylate intoxication

Pediatrics Group Issues New Guidance on Recess for the First Time in 13 Years

Guidelines come after years of shrinking recesses and worsening children's health

Medicaid Expansion Tied to Lower Mortality Among Young Adults With Kidney Failure

— Cohort study focused on 1-year mortality among 19- to 23-year-olds starting dialysis

Pediatricians Prepared to Manage Mood Disorders With SSRI

Pediatricians have reported feeling less comfortable discussing emotional regulation skills, cognitive behavioral therapy, or second-line medications with families.

US FDA Says Testing Reveals Domestic Infant Formula Supply Is Safe

The U.S. Food and Drug Administration on Wednesday said tested samples of infant formula available in the country contained very low levels of ⁠contaminants, confirming that...

Recommended News For You

CAR-T cell therapy for cancer causes 'brain fog,' study shows

Paging Dr. AI; Myth Busting in Cancer; Oncologists Shine in Malpractice Survey

Study suggests around 40% of postmenopausal hormone positive breast cancers are linked to excess body fat

AI tool automates liver tumor detection and monitoring

New clinical recommendation for local treatment of oligometastatic lung cancer.

Merck enhances its oncology pipeline by means of a strategic alliance with Hengrui.

Study Supports Lactated Ringer Solution for Fluid Resuscitation in SCD

Recommended Articles For You

Beyond the Standard: Personalized Cancer Vaccines and the Dawn of a New Era in Pediatric Oncology 

Unlocking the Secrets of Hemoglobin: Exploring the Wonders of Life-Sustaining Iron Compounds 

Impact of Hormone Therapy Cessation on Tumor Growth: Case Study of Ki-67 Reduction 

Interpreting Iron Studies: What Your Blood Results Really Mean  

Whats more on Hidoc Dr.

Medical Updates
KOL Videos
Surveys
Events

Daily news to keep you up to date

Gain valuable insights with our in-depth KOL Video discussions

Participate and win cash vouchers

Get updates on the latest events happening around the world
Featured News
Featured Articles
Featured Events
Featured KOL Videos

1.

Does pollution cause cancer?

2.

AI is equally capable of reading breast cancer scans as human radiologists.

3.

EVP Beats Cisplatin for Resectable MIBC

4.

New research points out a promising strategy for treating metastatic medulloblastoma

5.

Academics + Pharma = Big Bucks; New CAR-T Warnings; Patients Seek Cancer Tests.

1.

A Closer Look at Breast Cancer: Examining the Ultrasound Images

2.

Unlocking the Secrets of Oral Cancer Staging: A New Approach to Early Detection

3.

Impact of Hormone Therapy Cessation on Tumor Growth: Case Study of Ki-67 Reduction

4.

Unraveling the Mysteries of Lymphoma: A Journey into the Unknown

5.

Refining AML Survival: Prognostic Factors, Therapies, and Stem Cell Strategies Reviewed

1.

International Lung Cancer Congress®

2.

Genito-Urinary Oncology Summit 2026

3.

Future NRG Oncology Meeting

4.

ISMB 2026 (Intelligent Systems for Molecular Biology)

5.

Annual International Congress on the Future of Breast Cancer East

1.

Navigating the Complexities of Ph Negative ALL - Part III

2.

A Comprehensive Guide to First Line Management of ALK Positive Lung Cancer - Part VIII

3.

Management of 1st line ALK+ mNSCLC (CROWN TRIAL Update)

4.

Expert Group meeting with the management of EGFR mutation positive NSCLC - Part III

5.

Virtual Case Study on Pedal Edema and Triple Vessel Disease - An Initiative by Hidoc Dr.

Fastest Growing Medical Platform for Doctors

Address :
Hidoc Dr. Inc. | Delaware C Corp | 1309 Coffeen Ave. Suite 1200, Sheridan WY, 82801

Phone :
+1-415-463-3094

Email :
anishagadia@hidoc.co

Quick Links

Drug DatabaseDrug InteractionDiseases Database
KOL VideosKnowledge HubQuizzes
Medical UpdatesEventsAbout Us

© Copyright 2026 Hidoc Dr. Inc.

Terms & Conditions - LLP | Inc. | Privacy Policy - LLP | Inc. | Account Deactivation
Home
Profile
Login
bot