Gene therapy delivered early can help children with rare neurodegenerative disease retain motor and cognitive functions

Published Date: 25 Apr 2025

If administered early, gene therapy has the potential to change the medical history of children born with metachromatic leukodystrophy (MLD), a rare and lethal neurodegenerative disease of genetic origin which leads to the ...

Read Full News

Latest News

UK Commits $26.87 Million to Contain Ebola Outbreak in DRC

Britain has allocated up to 20 million pounds ($26.87 million) in ⁠new aid funding to help contain an Ebola outbreak in eastern ⁠Democratic Republic of the Congo, the UK's...

US Working With Small Biotech Firm on Experimental Ebola Treatment, HHS Official Says

U.S. officials are working with Mapp Biopharmaceutical to make an experimental Ebola treatment available for people who may have been exposed to ⁠the virus, an HHS official...

Congenital CMV Linked to Substantial Long-Term Health Issues

An analysis conducted in an integrated healthcare system provided insights into the long-term healthcare burden of cCMV infection.

Why the Test-Negative Design Is Our Most Vital Tool for Vaccine Effectiveness

Dr Daskalakis explains vaccine study designs and how the science of test negative design, a decades-old, tried and true design, is now being called into question.

Test Shortages Slow Fight Against Ebola in Congo, WHO Official Says

Six tons of medical supplies to fight Ebola are set to arrive in the Democratic Republic of Congo on Tuesday, ⁠but limited testing capacity was slowing the response to the...

Bird Flu Found in Polar Bear in Europe for First Time

Bird flu has been detected in a dead polar bear in the ⁠Arctic Svalbard archipelago, the first time the virus has been found in the species in ⁠Europe.

Todays Updates

EMA Backs Breast Cancer SERD After FDA No Vote

The recommendation follows phase 3 data showing longer progression-free survival when patients switched to camizestrant plus a CDK4/6 inhibitor.

Datopotamab Deruxtecan Earns New Breast Cancer Indication

The antibody drug conjugate was approved by the FDA for certain patients with triple-negative breast cancer.

Todays Updates

EMA Backs Breast Cancer SERD After FDA No Vote

The recommendation follows phase 3 data showing longer progression-free survival when patients switched to camizestrant plus a CDK4/6 inhibitor.

Datopotamab Deruxtecan Earns New Breast Cancer Indication

The antibody drug conjugate was approved by the FDA for certain patients with triple-negative breast cancer.

Latest News

Britain has allocated up to 20 million pounds ($26.87 million) in ⁠new aid funding to help contain an Ebola outbreak in eastern ⁠Democratic Republic of the Congo, the UK's...

U.S. officials are working with Mapp Biopharmaceutical to make an experimental Ebola treatment available for people who may have been exposed to ⁠the virus, an HHS official...

An analysis conducted in an integrated healthcare system provided insights into the long-term healthcare burden of cCMV infection.

Dr Daskalakis explains vaccine study designs and how the science of test negative design, a decades-old, tried and true design, is now being called into question.

Six tons of medical supplies to fight Ebola are set to arrive in the Democratic Republic of Congo on Tuesday, ⁠but limited testing capacity was slowing the response to the...

Bird flu has been detected in a dead polar bear in the ⁠Arctic Svalbard archipelago, the first time the virus has been found in the species in ⁠Europe.

News All Time

Biomarkers Spot Invasive Aspergillosis Post-Lung Transplant

RNA testing may help assess the consequences of common environmental mold.

South Africa: Brit With Hantavirus Gradually Improving

The condition of a British man who was admitted ⁠to a hospital in Johannesburg after falling ill with hantavirus aboard ⁠a luxury cruise ship is gradually improving.

Pregnancy vs Postpartum Flare Rates Differ in RA and SpA

Patients with rheumatoid arthritis are more likely to experience flares during the early postpartum period than during pregnancy; however, flare rates in those with spondyloarthritis remain stable.

WHO Says Seven Cases Of Hantavirus Confirmed From Cruise Ship

Seven cases of the ⁠Andes hantavirus have now been confirmed among people ⁠who were passengers on board the ⁠cruise ship, the ‌World Health Organization said on...

A Child's First Flu May Set the Tone for Immunity

New research shows that a child's earliest encounter with the virus can 'imprint' the immune system, shaping how their antibodies respond to future infections.

First Lyme Vaccine in Decades Nears Approval

Positive phase 3 findings may reshape Lyme disease prevention among people with frequent tick exposure across endemic regions.

Prior Maternal Syphilis Boosts Congenital Infection Risk

A history of adequately treated syphilis before pregnancy is associated with more than a 100-fold increase in congenital syphilis risk.

Telemedicine in Pediatric Care Tied to Lower Antibiotic Use

Primary care telemedicine visits for acute respiratory tract infections in children are associated with a lower rate of antibiotic prescriptions than in-person visits.

US CDC Classifies Hantavirus Outbreak as 'level 3' Emergency Response, ABC News Reports

The ⁠U.S. Centers ⁠for Disease ⁠Control and ‌Prevention has classified the hantavirus ‌outbreak as 'level 3' ‌emergency ‌response, the ⁠lowest ‌level ⁠of emergency...

Does Mycoplasma genitalium Cause Recurrent Preterm Birth?

Mycoplasma genitalium infection shows an association with prior spontaneous preterm birth but does not increase the risk for recurrent spontaneous preterm birth.

Moderna's MRNA Flu Vaccine Outperforms Standard Shot in Late-stage Trial

Moderna's mRNA-based seasonal flu vaccine worked better than conventional flu shots in a late-stage international trial of more than 40,000 adults aged ⁠50 and older,...

CDC Says It Is Monitoring US Travelers on Cruise Ship After Hantavirus Outbreak

The United States is closely monitoring the situation with U.S. travelers on board the luxury cruise ship that was ⁠hit by a hantavirus outbreak, the Centers for Disease...

US FDA Blocked Publication of COVID, Shingles Vaccine Safety Studies

Officials at the U.S. Food and Drug Administration blocked the publication of several studies supporting the ⁠safety of widely used vaccines against COVID-19 and shingles, a...

New Surveillance Study Supports Maternal RSV Vaccine Safety

Early data keep hypertension concerns on the radar, but more robust research shows no increased risk.

California's Highest Court Leans Toward Gilead in Considering Drugmakers' 'duty to Innovate'

California's highest court on Wednesday appeared skeptical of requiring Gilead Sciences and other manufacturers of drugs that are considered safe to try developing drugs...

Young Age, Lower BMI May Predict HIV Treatment Failure

Younger age, lower BMI for age, and lower CD4% at antiretroviral therapy initiation may predict treatment failure in children living with HIV.

Recommended News For You

Shorter, less intense regimen still effective for HPV-linked throat cancer, study shows

Adopted cancer cells and the effects of their presence.

Combo Therapy Boosts Early CML Response but Not Long Term

Pickleball program boosts health and wellness for cancer survivors, study finds

Sustained reduction found in prostate cancer mortality with prostate-specific antigen screening

"We Caught It Early": Advantage or Disadvantage?

From 40 to 74, the US Preventive Services Task Force advises every two years for screening mammography.

Recommended Articles For You

Screening Efficacy, Molecular Precision, and Therapeutic Revolutions in Lung Cancer 2025 

Everything You Need To Know About Melanoma Choroid: Causes, Symptoms, and Treatment 

Uncovering the Hidden Picture: Using Ultrasound to Diagnose Breast Cancer 

The Significance of APTT Blood Test Results for Detecting Coagulation Disorders 

Whats more on Hidoc Dr.

Medical Updates
KOL Videos
Surveys
Events

Daily news to keep you up to date

Gain valuable insights with our in-depth KOL Video discussions

Participate and win cash vouchers

Get updates on the latest events happening around the world
Featured News
Featured Articles
Featured Events
Featured KOL Videos

1.

Non-Factor Therapies in Hemophilia: Cutting-Edge Approaches to Individualize Care

2.

FDA approves Blenrep for relapsed or refractory multiple myeloma

3.

X-ray and radar technology combined to reduce cancer screening risks

4.

Extended Maintenance with Imatinib Enhances Disease-Free Survival in High-Risk GIST.

5.

Researchers discuss HER2-low and HER2-zero in breast cancer

1.

Understanding Mesenteric Masses: Symptoms, Diagnosis, and Treatment Options

2.

Liposomal Doxorubicin and Mitomycin in Modern Cancer Treatment

3.

The New Era of Oncology: Key Updates and Clinical Insights

4.

HIPEC in Platinum-Sensitive Ovarian Cancer: A Promising Yet Controversial Option

5.

Theranostics and Radioligand Therapy: Precision Cancer Care with Targeted Radionuclides

1.

International Lung Cancer Congress®

2.

Genito-Urinary Oncology Summit 2026

3.

Future NRG Oncology Meeting

4.

ISMB 2026 (Intelligent Systems for Molecular Biology)

5.

Annual International Congress on the Future of Breast Cancer East

1.

Exploring Potentials of Lorlatinib: The Third Generation ALK-TKI Through CROWN Trial

2.

Managing ALK Rearranged Non-Small Cell Lung Cancer with Lorlatinib - Part I

3.

Breaking Ground: ALK-Positive Lung Cancer Front-Line Management - Part V

4.

A Comprehensive Guide to First Line Management of ALK Positive Lung Cancer - Part II

5.

Expert Group meeting with the management of EGFR mutation positive NSCLC - Part III

Fastest Growing Medical Platform for Doctors

Address :
Hidoc Dr. Inc. | Delaware C Corp | 1309 Coffeen Ave. Suite 1200, Sheridan WY, 82801

Phone :
+1-415-463-3094

Email :
anishagadia@hidoc.co

Quick Links

Drug DatabaseDrug InteractionDiseases Database
KOL VideosKnowledge HubQuizzes
Medical UpdatesEventsAbout Us

© Copyright 2026 Hidoc Dr. Inc.

Terms & Conditions - LLP | Inc. | Privacy Policy - LLP | Inc. | Account Deactivation
Home
Profile
Login
bot