Increased Frataxin Levels in Friedreich Ataxia Following CT-1601 Treatment, Performed in a Phase 2 Trial.

Published Date: 06 Aug 2023

The FDA has received encouraging data from the 25 mg cohort study investigating Larimar Therapeutics' CTI-1601. The FDA and Larimar Therapeutics have scheduled a meeting for later this quarter to discuss the next steps for a phase 2 trial.

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