The FDA has approved the first gene therapy for the treatment of metachromatic leukodystrophy in children.

Published Date: 21 Mar 2024

As a result of the ruling, atidarsagene autotemcel is now the first gene therapy for MLD, a rare genetic condition affecting the brain and nervous system, to receive FDA approval.

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U.S. Senator Dick Durbin urged Health Secretary Robert F. Kennedy Jr. on Wednesday to resist an easing of rules on ⁠flavoured vapes, saying the moves were short-sighted and...

U.S. Health Secretary Robert F. Kennedy Jr. fired the chair and vice chair of the influential task force that decides what preventive medical care should be ⁠provided at no...

Spinal anesthesia offers faster recovery, similar OR time, and significantly less opioid use, with no increase in cost or OR delays.

Though no association was seen between eating a vegetarian diet and nutrition risk, there were too few vegan children in the study to assess their nutrition risk.

A universal prenatal and infant cash prescription program was associated with a decrease in investigated maltreatment allegations within the first 6 months of life.

The ITP Expert Exchange: Translating Evidence Into Evolving Practice

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