In the Phase 1/2 ASPIRO Trial, gene therapy AT132 improves ventilator dependence in patients with X-linked myotubular myopathy.

Published Date: 17 Dec 2023

More than half of dosed pediatric patients with X-linked myotubular myopathy learned to use a ventilator independently, and some even learned to walk on their own, according to new preliminary data.

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The FDA has approved a radioactive agent for use ⁠in brain scans to help assess patients for Alzheimer's disease.

Patients who undergo anterior cruciate ligament reconstruction may show persistent neuromuscular alterations during functional tasks, despite reduced joint position sense errors.

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Standard cognitive screening thresholds may exclude many patients with biomarker-confirmed atypical Alzheimer’s disease despite early-stage functional impairment, new data show.

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