FDA approves sepiapterin to treat phenylketonuria in adult, pediatric patients

Published Date: 07 Aug 2025

“Without treatment, individuals with PKU would have very high blood Phe levels...so that results in neurocognitive deficits and mood disorders," Suzanne Hollander, MS, RD, LDN, said.

Read Full News

Latest News

Aprepitant Eases Cannabinoid Hyperemesis Syndrome in Teens

Hospitalized adolescents had a shorter stay and speedier symptom resolution with this adjunctive therapy.

Taylor Farms Recalls Salsa, Guacamole on Salmonella Outbreak, Intensifying Food-safety Fears

Taylor Farms is recalling prepared foods containing jalapenos from retailers including Walmart and Whole Foods in several states over potential salmonella contamination, the...

Distinguish Support Gaps From Caregiver Neglect, Docs Urged

Too often, clinicians add medications, appointments, and treatments without considering the cumulative burden has become unmanageable.

Hearing Screening For Preemies May Predict Cognition

Infants born extremely premature who do not pass newborn hearing screening assessments show lower scores on language and cognitive assessments at age 2.

Adults Born Very Preterm Show Distinct Functioning Profiles

Adults born very preterm or with very low birth weight show varied functioning profiles in adulthood, with a higher childhood intelligence quotient associated with positive functioning in adulthood.

Milk, Breastfeeding, and Teeth: What the Evidence Shows

Unsweetened dairy may help protect enamel, but added sugar can erase the benefit. Breastfeeding and milk alternatives also have surprising age- and product-specific effects.

Todays Updates

Hyponatremia Risk Varies Among Second-Gen Antipsychotics

Aripiprazole is associated with a lower risk for hyponatremia compared with olanzapine in patients treated with second-generation antipsychotics, a new cohort study shows.

HCT Survival Outcomes Improving in Relapsed Hodgkin Lymphoma

Researchers evaluate changes in post-transplantation outcomes among patients with relapsed or refractory Hodgkin lymphoma from 2010 to 2022.

How Much of a Cancer Drug Is Too Much?

In a recent KFF survey, 43% of US adults said they had skipped their medication in the past year because of cost.

Todays Updates

Hyponatremia Risk Varies Among Second-Gen Antipsychotics

Aripiprazole is associated with a lower risk for hyponatremia compared with olanzapine in patients treated with second-generation antipsychotics, a new cohort study shows.

HCT Survival Outcomes Improving in Relapsed Hodgkin Lymphoma

Researchers evaluate changes in post-transplantation outcomes among patients with relapsed or refractory Hodgkin lymphoma from 2010 to 2022.

How Much of a Cancer Drug Is Too Much?

In a recent KFF survey, 43% of US adults said they had skipped their medication in the past year because of cost.

Latest News

Hospitalized adolescents had a shorter stay and speedier symptom resolution with this adjunctive therapy.

Taylor Farms is recalling prepared foods containing jalapenos from retailers including Walmart and Whole Foods in several states over potential salmonella contamination, the...

Too often, clinicians add medications, appointments, and treatments without considering the cumulative burden has become unmanageable.

Infants born extremely premature who do not pass newborn hearing screening assessments show lower scores on language and cognitive assessments at age 2.

Adults born very preterm or with very low birth weight show varied functioning profiles in adulthood, with a higher childhood intelligence quotient associated with positive functioning in adulthood.

Unsweetened dairy may help protect enamel, but added sugar can erase the benefit. Breastfeeding and milk alternatives also have surprising age- and product-specific effects.

News All Time

Advancing Pediatric Hemophilia Care in the Non-Factor Era: Individualizing Prophylaxis

Advancing Pediatric Hemophilia Care in the Non-Factor Era: Individualizing Prophylaxis

Advancing Pediatric Hemophilia Care in the Non-Factor Era: From Factor Replacement to Rebalancing Therapies

Advancing Pediatric Hemophilia Care in the Non-Factor Era: From Factor Replacement to Rebalancing Therapies

Non-Factor Therapies in Hemophilia: Cutting-Edge Approaches to Individualize Care

Non-Factor Therapies in Hemophilia: Cutting-Edge Approaches to Individualize Care

Newborn Girls Appear Less Likely to Get Vitamin K, Hepatitis B Shots

Relationship stronger for vitamin K; may be tied to circumcision

AAP Disputes Kennedy's Claim That Vaccine Panel Can't Meet Ahead of Flu Season

The federal government can "restore a lawful ACIP" and meet "at any time," AAP president says

RFK Jr. Goes After Journal That Removed Vaccine Study

"The paper's title tells you it shouldn't be published," said vaccine researcher Paul Offit

Outbreak Kills Over 200; ACIP Investigation Launched; Hackers Demand $75M From Novo

Health news and commentary gathered by MedPage Today staff

Over 770,000 Kids No Longer Receiving SNAP Benefits After Trump Changes Food Program

Arizona has seen the nation's largest percentage decline in SNAP participants

Generic Single-Dose Flu Antiviral Gets FDA's Blessing

Studies have shown baloxavir to be a standout among antivirals commonly used for influenza

Utah Marks a Year of Battling Measles, With No Clear End in Sight

Outbreaks will likely affect whether the U.S. can keep its measles-free designation

The Knicks Just Gave Us a Teaching Moment. Let's Not Waste It.

This historic win offers valuable lessons for young people's mental health

Shorter TB Regimen Matched Standard Care in Rifampicin-Resistant Disease

Protocol can be used in children and pregnant women

The Truth About 'Looksmaxxing'

Dr. Mike addresses the online epidemic affecting teen boys

New Charter Unveiled for CDC's Influential Vaccine Committee

Changes to rules governing ACIP could inject more politicization, experts warn

'Tiniest Penis' Fundraiser; Flu Vaccine Maker Investigated; FDA Rejects Gout Drug

Health news and commentary gathered by MedPage Today staff

Efforts to End School Vaccine Mandates Hit a Wall in Florida

The outcome could offer insights into such efforts' chances in other states

Recommended News For You

AI Breath Test IDs Cancers; More Grief for Prior Auth; Imatinib Discoverer Resigns

Sickle Cell Disease Drug Pulled From Global Markets

After two years, a significant left nasal obstruction was finally diagnosed.

Axatilimab Demonstrates Effectiveness in Refractory/Recurrent GVHD.

Glioblastoma cells can 'unstick' from their neighbors to become more deadly

Anticoagulation for 12 months has been found to improve outcomes in cancer patients with minor blood clots.

enhancing survivors of brain tumors' quality of life.

Recommended Articles For You

Strategic Standards in Hematology for Specialists 

Metabolic Vulnerabilities in Solid Tumor Progression 

Revolutionizing Cancer Treatment: Harnessing the Power of AI in Histopathology 

Understanding Melanoma: From Diagnosis to Healing and Excision in Denver 

Whats more on Hidoc Dr.

Medical Updates
KOL Videos
Surveys
Events

Daily news to keep you up to date

Gain valuable insights with our in-depth KOL Video discussions

Participate and win cash vouchers

Get updates on the latest events happening around the world
Featured News
Featured Articles
Featured Events
Featured KOL Videos

1.

Q&A: When will individuals be able to receive customized cancer vaccines?

2.

Canadian Group Calls for Earlier Colorectal Cancer Screening

3.

Children living near oil and gas wells face higher risk of rare leukemia, studies show

4.

Researchers achieve a significant milestone in the management of anemia in chronic lymphocytic leukemia.

5.

Talquetamab Combos Show Survival Benefit in r/r Myeloma

1.

Liquid Biopsy: A Revolutionary Tool for Early Detection and Monitoring of Colorectal Cancer

2.

Clinical Pharmacology of Megakaryocyte Maturation-Targeted Therapeutics

3.

The Benefits and Side Effects of Bortezomib in the Fight Against Cancer 

4.

Personalized Tumor Ecological Landscapes in Oncology

5.

Unmasking the Subtle Symptoms of Colon Cancer

1.

Asian Symposium on Advancement in Hematology and Oncology (ASAHO)

2.

International Cancer Conference

3.

Asian Symposium on Advancement in Hematology and Oncology (ASAHO)

4.

Asian Symposium on Advancement in Hematology and Oncology

5.

Asian Symposium on Advancement in Hematology and Oncology

1.

Lorlatinib in the Management of 1st line ALK+ mNSCLC (CROWN TRIAL Update)

2.

Pazopanib Takes Center Stage in Managing Renal Cell Carcinoma - Part II

3.

Current Scenario of Cancer- Q&A Session to Close the Gap Part II

4.

Cost Burden/ Burden of Hospitalization For R/R ALL Patients

5.

Immunotherapy: A New Era in Cancer Treatment

Fastest Growing Medical Platform for Doctors

Address :
Hidoc Dr. Inc. | Delaware C Corp | 1309 Coffeen Ave. Suite 1200, Sheridan WY, 82801

Phone :
+1-415-463-3094

Email :
anishagadia@hidoc.co

Quick Links

Drug DatabaseDrug InteractionDiseases Database
KOL VideosKnowledge HubQuizzes
Medical UpdatesEventsAbout Us

© Copyright 2026 Hidoc Dr. Inc.

Terms & Conditions - LLP | Inc. | Privacy Policy - LLP | Inc. | Account Deactivation
Home
Profile
Login
bot