FDA approves sepiapterin to treat phenylketonuria in adult, pediatric patients

Published Date: 07 Aug 2025

“Without treatment, individuals with PKU would have very high blood Phe levels...so that results in neurocognitive deficits and mood disorders," Suzanne Hollander, MS, RD, LDN, said.

Read Full News

Latest News

US Senator Durbin Urges RFK Jr. to Resist Easing Vape Rules

U.S. Senator Dick Durbin urged Health Secretary Robert F. Kennedy Jr. on Wednesday to resist an easing of rules on ⁠flavoured vapes, saying the moves were short-sighted and...

US Health Secretary Kennedy Fires Heads Of Key Preventive Health Panel

U.S. Health Secretary Robert F. Kennedy Jr. fired the chair and vice chair of the influential task force that decides what preventive medical care should be ⁠provided at no...

Spinal Anesthesia for Circumcision Tops General Anesthesia

Spinal anesthesia offers faster recovery, similar OR time, and significantly less opioid use, with no increase in cost or OR delays.

Vegetarian Diet in Kids Not Linked to More Nutrition Risk

Though no association was seen between eating a vegetarian diet and nutrition risk, there were too few vegan children in the study to assess their nutrition risk.

Cash Transfers Cut Infant Maltreatment Reports

A universal prenatal and infant cash prescription program was associated with a decrease in investigated maltreatment allegations within the first 6 months of life.

The ITP Expert Exchange: Translating Evidence Into Evolving Practice

The ITP Expert Exchange: Translating Evidence Into Evolving Practice

Todays Updates

EMA Backs Breast Cancer SERD After FDA No Vote

The recommendation follows phase 3 data showing longer progression-free survival when patients switched to camizestrant plus a CDK4/6 inhibitor.

Datopotamab Deruxtecan Earns New Breast Cancer Indication

The antibody drug conjugate was approved by the FDA for certain patients with triple-negative breast cancer.

Todays Updates

EMA Backs Breast Cancer SERD After FDA No Vote

The recommendation follows phase 3 data showing longer progression-free survival when patients switched to camizestrant plus a CDK4/6 inhibitor.

Datopotamab Deruxtecan Earns New Breast Cancer Indication

The antibody drug conjugate was approved by the FDA for certain patients with triple-negative breast cancer.

Latest News

U.S. Senator Dick Durbin urged Health Secretary Robert F. Kennedy Jr. on Wednesday to resist an easing of rules on ⁠flavoured vapes, saying the moves were short-sighted and...

U.S. Health Secretary Robert F. Kennedy Jr. fired the chair and vice chair of the influential task force that decides what preventive medical care should be ⁠provided at no...

Spinal anesthesia offers faster recovery, similar OR time, and significantly less opioid use, with no increase in cost or OR delays.

Though no association was seen between eating a vegetarian diet and nutrition risk, there were too few vegan children in the study to assess their nutrition risk.

A universal prenatal and infant cash prescription program was associated with a decrease in investigated maltreatment allegations within the first 6 months of life.

The ITP Expert Exchange: Translating Evidence Into Evolving Practice

News All Time

RFK Jr. Faced Congress. A Physician-Senator's Competing Loyalties Were on Display.

Bill Cassidy, who is seeking reelection, walked a fine line

Vaccines, Budget Cuts, Affordability: Takeaways From RFK Jr.'s Gauntlet of Hearings

Kennedy acknowledged some HHS cuts are "painful"

Kids With Chronic Health, Social Needs More Likely to Frequently Miss School

Weighted study sample represented more than 49 million U.S. kids

South Carolina's Measles Outbreak Is Over After Sickening Nearly 1,000 People

But health officials are still on guard

FDA Analysis Says Infant Formula Supply Is Safe After Testing for Contaminants

"There's no reason not to use any available formula," said one expert

Chocolate Product Recall; Trump Admin Fights Vaccine Ruling; Measles in Travelers

Health news and commentary gathered by MedPage Today staff

New Maintenance Option Approved for Asthma

Breztri becomes the first single-inhaler triple therapy for patients as young as 12 years

Trump's New Surgeon General Pick Has Both Praised and Cringed at His Administration

Nicole Saphier is a radiologist and former Fox News Channel contributor

Telemedicine Visits Tied to Fewer Antibiotics for Respiratory Infections

Findings for virtual visits with primary care suggested high quality

This Common Household Product Tied to Kid's Seizures

Investigation revealed the likely cause of salicylate intoxication

Teen Seeks Care for Delayed Growth Compared With His Twin

Case shows confluence of hormone therapy cost and limited resources in developing areas

Did Newborn Die From Mom's Marijuana Use?

Diagnosis of exclusion leads to answer of... probably

Medicaid Expansion Tied to Lower Mortality Among Young Adults With Kidney Failure

— Cohort study focused on 1-year mortality among 19- to 23-year-olds starting dialysis

Pediatrics Group Issues New Guidance on Recess for the First Time in 13 Years

Guidelines come after years of shrinking recesses and worsening children's health

Pediatricians Prepared to Manage Mood Disorders With SSRI

Pediatricians have reported feeling less comfortable discussing emotional regulation skills, cognitive behavioral therapy, or second-line medications with families.

US FDA Says Testing Reveals Domestic Infant Formula Supply Is Safe

The U.S. Food and Drug Administration on Wednesday said tested samples of infant formula available in the country contained very low levels of ⁠contaminants, confirming that...

Recommended News For You

Safe and acceptable telehealth suicide prevention program.

AI Breath Test IDs Cancers; More Grief for Prior Auth; Imatinib Discoverer Resigns

Limited Benefit from New Drugs; Significant Increase in Drug Prices; AI Boost for Mammo Results.

Housing aid linked to lower medical financial hardship among US renters with cancer

High Rate of Surgical Success in Complex NSCLC With Neoadjuvant Chemoimmunotherapy

According to research, the mineralization of the bone matrix controls the growth of tumor cells.

Herpes virus-based vaccine shows promise in targeting tumors without side effects

Recommended Articles For You

Uncovering the Hidden Signs: How to Recognize the Early Symptoms of Colon Cancer 

Navigating the Complexity of Peritoneal Carcinomatosis: A Guide for Patients and Caregivers 

Unlocking the Potential of Hemin: A Novel Approach to Health and Wellbeing 

Amivantamab Plus Chemotherapy Outperforms Standard Care in Post-Osimertinib NSCLC 

Whats more on Hidoc Dr.

Medical Updates
KOL Videos
Surveys
Events

Daily news to keep you up to date

Gain valuable insights with our in-depth KOL Video discussions

Participate and win cash vouchers

Get updates on the latest events happening around the world
Featured News
Featured Articles
Featured Events
Featured KOL Videos

1.

Potential targets for treating the most common type of liver cancer in children have been identified by a collaborative study.

2.

Study identifies new approach to protect the brain during radiation therapy

3.

While most cancer screenings won't prolong lives, there are still good reasons to continue screening.

4.

Chemo-Free Quadruplet Shows Promise as DLBCL's First Therapy.

5.

Radiation therapy for patients with breast cancer

1.

Radiation in Oncology: Advances, Applications, and Accessibility

2.

The Next Generation of Precision: How Multi-Specific Antibodies are Redefining Oncology's Future - A 2025 Review

3.

Cracking Oncology Drug Resistance: New Strategies to Overcome Challenges in Modern Cancer Therapy

4.

Unlocking the Secrets of Neutrophils: Exploring Their Role in Immune Defense

5.

Precision Oncology: Personalized Medicine Shaping the Future of Cancer Care

1.

International Lung Cancer Congress®

2.

Genito-Urinary Oncology Summit 2026

3.

Future NRG Oncology Meeting

4.

ISMB 2026 (Intelligent Systems for Molecular Biology)

5.

Annual International Congress on the Future of Breast Cancer East

1.

Pazopanib Takes Center Stage in Managing Renal Cell Carcinoma - Part II

2.

Recent Data Analysis for First-Line Treatment of ALK+ NSCLC

3.

Navigating the Complexities of Ph Negative ALL - Part XIII

4.

Navigating the Complexities of Ph Negative ALL - Part IV

5.

Revolutionizing Treatment of ALK Rearranged NSCLC with Lorlatinib - Part VIII

Fastest Growing Medical Platform for Doctors

Address :
Hidoc Dr. Inc. | Delaware C Corp | 1309 Coffeen Ave. Suite 1200, Sheridan WY, 82801

Phone :
+1-415-463-3094

Email :
anishagadia@hidoc.co

Quick Links

Drug DatabaseDrug InteractionDiseases Database
KOL VideosKnowledge HubQuizzes
Medical UpdatesEventsAbout Us

© Copyright 2026 Hidoc Dr. Inc.

Terms & Conditions - LLP | Inc. | Privacy Policy - LLP | Inc. | Account Deactivation
Home
Profile
Login
bot