Phase 3 of FORTIFY for Limb-Girdle Muscular Dystrophy Type 2i saw the beginning of dosing.

Published Date: 13 Aug 2023

The FDA and BridgeBio Pharma met to discuss the use of glycosylated -dystroglycan levels as a surrogate end point for the phase 3 trial FORTIFY investigating BBP-418. BridgeBio Pharma believes there is a chance for an accelerated approval.

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