Evaluation of AOC 1001's Therapeutic Potential in Myotonic Dystrophy Type 1 Patients.

Published Date: 16 Nov 2023

The chief medical officer of Avidity, Steve Hughes, MD, offered insight into the recently released positive phase 1/2 and OLE data assessing AOC 1001, an experimental antisense oligonucleotide, in individuals suffering from myotonic dystrophy type 1.

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