FDA Grants RMAT Designation to ATSN-201 Gene Therapy for XLRS

Published Date: 18 Apr 2025

FDA Grants RMAT Designation to ATSN-201 Gene Therapy for XLRS

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A treatment that targets dysfunctional photoreceptors regardless of the underlying genetic mutation leads to improved functional vision in advanced severe vision loss.

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Beyond Intravitreal Injections: Advancing Retinal Vascular Disease Care With Sustained Delivery Therapies

Focus Aligned: Patient Selection and Counseling for Pharmacologic Presbyopia Therapies

Focus Reengineered: Mechanisms and Clinical Data for Pharmacologic Presbyopia Therapies

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