Limb-girdle muscular dystrophy type 2I/R9 Phase 1/2 Gene Therapy Trial Patient Dosing Began.

Published Date: 10 Aug 2023

14 people with genetically confirmed limb-girdle muscular dystrophy are anticipated to participate in the study, and they will be randomly assigned to receive either AB-1003 or a placebo for a full year of treatment.

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