For mutations amenable to exon 44 skipping, the FDA designates Duchenne Agent AOC 1044 as a Rare Pediatric Disease.

Published Date: 23 May 2024

In the second part of 2024, Avidity Biosciences plans to release new cohort data from the phase 1/2 EXPLORE44 trial, which evaluated AOC 1044 in Duchenne muscular dystrophy mutations susceptible to exon 44 skipping.

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