In heavier pediatric SMA patients, intravenous Zolgensma improves motor function.

Published Date: 10 Mar 2024

Results from the most recent phase 3b SMART trial, in which patient weights range from 8.5 kg to 21 kg, confirm the safety and effectiveness of intravenous onasemnogene abeparvovec (Zolgensma; Novartis) in treating spinal muscular atrophy.

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