Findings from the phase 3 TransportNPC study showed that Trappsol Cyclo missed the primary end point in Niemann-Pick type C, but subgroup and survival data support planned 2026 NDA.

NeurologyLive® Friday 5 — October 2, 2026 Isabella Ciccone, MPH

Take 5 minutes to catch up on NeurologyLive®'s highlights from the week ending October 2, 2026.

Todays Updates

Trappsol Cyclo Misses Primary End Point in Phase 3 Trial for Niemann-Pick Disease Type C Isabella Ciccone, MPH

Findings from the phase 3 TransportNPC study showed that Trappsol Cyclo missed the primary end point in Niemann-Pick type C, but subgroup and survival data support planned 2026 NDA.

NeurologyLive® Friday 5 — October 2, 2026 Isabella Ciccone, MPH

Take 5 minutes to catch up on NeurologyLive®'s highlights from the week ending October 2, 2026.

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Todays Updates

Trappsol Cyclo Misses Primary End Point in Phase 3 Trial for Niemann-Pick Disease Type C Isabella Ciccone, MPH

NeurologyLive® Friday 5 — October 2, 2026 Isabella Ciccone, MPH

Todays Updates

Trappsol Cyclo Misses Primary End Point in Phase 3 Trial for Niemann-Pick Disease Type C Isabella Ciccone, MPH

NeurologyLive® Friday 5 — October 2, 2026 Isabella Ciccone, MPH

Latest News

News All Time

US Regulators Urge More Research on Testosterone Therapy for Women as Experts Debate Benefits, Risks

FDA Grants Priority Review for Diabetic Foot Ulcer Therapy

Pennsylvania Measles Cases Top 700 After Four Outbreak-related Deaths Reported

Fear of Relapse Burdens Patients With Vitiligo

Adding IVIG to Prednisone Boosts Outcomes in IIMs

Smoke Exposure Tied to HS Risk in Children and Teens

A Decade After Mercury Ban, Toxic Skin Bleachers Still Offered on Top Retailers' Websites

Pennsylvania Measles-associated Deaths Climb to Four as Outbreak Grows

FDA Grants Priority Review to Zasocitinib for Psoriasis

Serious Infections Lower With Anifrolumab in CLE Patients

COVID, 6 Years on: The Pandemic’s Long Clinical Shadow

Prior Keratinocyte Carcinoma Tied to Mucosal Melanoma

Trust in Measles Vaccines Falls in US, Reuters Ipsos Poll Finds

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